Walz was echoing a question that U.S. Army lawyer Joseph Welch posed to Republican U.S. Sen. Joseph McCarthy of Wisconsin ...
Crofelemer has been granted Orphan Drug Designation by the U.S. Food and Drug Administration (FDA) and the European Medicines Agency for SBS and MVID. In October 2025, as announced, the company ...
CK0804, a novel Treg therapy, gains FDA orphan drug status for myelofibrosis, promising new hope for patients with limited treatment options. CK0804, an investigational allogeneic regulatory T cell ...
"Cellenkos gains FDA orphan drug status for CK0804 to treat myelofibrosis" was originally created and published by ...
The American Society of Gene & Cell Therapy (ASGCT), the leading professional organization for the advancement of cell and gene therapies (CGTs), and the Orphan Therapeutics Accelerator (OTXL), a ...
A new drug application (NDA) has been submitted to the FDA seeking approval of rusfertide, an investigational hepcidin ...
Though the onset of cold weather has put a chill on many things Kansans like to do, here are five great stops for Kansas ...
This empirical study demonstrates that a multi-criteria decision analysis (MCDA) framework is a feasible and consistent supplementary tool for evaluating the value of orphan medicinal products (OMPs) ...
Top stories ranked by being the most-read A well explosion, a fatal accident, crime news and a disease impacting deer were ...
Paul Verdin, VP of consulting and analytics, and Andreas Hadjivasiliou, managing analyst at Evaluate, tell us about the company’s Orphan Drug Report 2022, which highlights activities within the orphan ...
With global population growth and climate change posing escalating threats to crop production, the current food system is ...
It seems fitting that this history of mental health ends with Oregon’s attempt to grapple with the needs of children and ...