Confirmed wild-type CFTR delivery and expression in conducting airway cells of patients with class I mutationsKB407 transduction confirmed in all ...

Confirmed wild-type CFTR delivery and expression in conducting airway cells of patients with class I mutations KB407 transduction confirmed in all six patients with successful bronchoscopies irrespect ...

SpliceBio, a clinical-stage genetic medicines company pioneering protein splicing to address diseases caused by mutations in ...

Seasoned biopharma industry leader brings more than 30 years of experience to support company’s growth trajectory —BERKELEY, Calif.--(BUSINESS WIRE)--Ray Therapeutics, a clinical-stage biotechnology ...

Innovative research into the gene-editing tool targets influenza’s ability to replicate—stopping it in its tracks.

A handful of crypto-powered health groups have cropped up, aiming to put patients in the driver's seat. Does this ...

Rare Pediatric Disease Priority Review Voucher (PRV) granted by FDA at approval to be transferred from Sentynl Therapeutics ...

These anime worlds aren’t just settings — they feel like places fans genuinely wish they could live in, explore, and for some ...

Being a child actor can be tough, but these young stars became grown up actors (and filmmakers) who ended up landing an Oscar ...

Neuroblastoma is a rare childhood cancer arising from immature nerve cells mainly affecting infants and toddlers due to ...

Rare Pediatric Disease Priority Review Voucher (PRV) granted by FDA at approval to be transferred from Sentynl Therapeutics to Cyprium Cyprium eligible to receive tiered royalties and up to $129 milli ...

Thousands of global Scots are using the Big Y‑700 DNA test to uncover clan ancestry, confirm deep Scottish roots and spark emotional journeys ...